FDA Approves Mitapivat for Thalassemia-Connected Anemia

FDA Approves Mitapivat for Thalassemia-Connected Anemia

MedPage This day) — The FDA accepted mitapivat (Aqvesme) as a disease-making improvements to remedy for anemia in adults with alpha- or beta-thalassemia, a uncommon inherited blood disease that affects hemoglobin production.
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